Category:Orphan drugs
From HandWiki
Here is a list of articles in the Orphan drugs category of the Chemistry portal.
Lists of all drugs that have received orphan status in the United States and Europe are available from the U.S. Food and Drug Administration and the European Commission, respectively:
Pages in category "Orphan drugs"
The following 200 pages are in this category, out of 451 total.
(previous page) (next page)A
- Biology:Acalabrutinib
- Chemistry:Acetohydroxamic acid
- Chemistry:Adagrasib
- Chemistry:Afamelanotide
- Chemistry:Afatinib
- Chemistry:Afegostat
- Chemistry:Alglucosidase alfa
- Chemistry:Alisporivir
- Biology:Allogeneic processed thymus tissue
- Chemistry:Alpha-1 antitrypsin
- Chemistry:Altretamine
- Chemistry:Alvocidib
- Chemistry:Amatuximab
- Chemistry:Ambrisentan
- Chemistry:Amifampridine
- Chemistry:Amikacin
- Chemistry:4-Aminopyridine
- Chemistry:Amitriptyline
- Chemistry:Anagrelide
- Chemistry:Ansuvimab
- Chemistry:Anti-CD22 immunotoxin
- Biology:Apadamtase alfa
- Chemistry:Artesunate
- Biology:Arylsulfatase B
- Chemistry:Asciminib
- Biology:Asfotase alfa
- Biology:Asparaginase
- Chemistry:Ataluren
- Chemistry:Atezolizumab
- Chemistry:Avacopan
- Chemistry:Avalglucosidase alfa
- Chemistry:Avapritinib
- Chemistry:Avatrombopag
- Chemistry:Avelumab
- Biology:Axicabtagene ciloleucel
- Chemistry:Azacitidine
B
- Chemistry:Baloxavir marboxil
- Chemistry:Bardoxolone methyl
- Chemistry:Belantamab mafodotin
- Chemistry:Belimumab
- Chemistry:Belumosudil
- Physics:Belumosudil
- Chemistry:Belzutifan
- Chemistry:Benralizumab
- Biology:Beremagene geperpavec
- Chemistry:Berotralstat
- Biology:Betibeglogene autotemcel
- Chemistry:Bevacizumab
- Chemistry:Binimetinib
- Chemistry:Birch bark
- Biology:Bis-choline tetrathiomolybdate
- Chemistry:Bortezomib
- Chemistry:Bosentan
- Chemistry:Brentuximab vedotin
- Biology:Brexucabtagene autoleucel
- Chemistry:Brigatinib
- Chemistry:Brincidofovir
- Biology:Bromelain (pharmacology)
- Chemistry:Budesonide
- Biology:Budesonide
- Chemistry:Bulevirtide
- Chemistry:Burosumab
- Chemistry:Busulfan
C
- Chemistry:C-Met inhibitor
- Chemistry:Cabozantinib
- Chemistry:Caffeine citrate
- Chemistry:Calaspargase pegol
- Chemistry:Cannabidiol
- Chemistry:Caplacizumab
- Chemistry:Capmatinib
- Chemistry:Carboprost
- Chemistry:Carglumic acid
- Chemistry:Carmustine
- Biology:Casimersen
- Chemistry:Catridecacog
- Chemistry:Cereblon E3 ligase modulator
- Chemistry:Cerliponase alfa
- Biology:CGTG-102
- Chemistry:Chlormethine
- Chemistry:Cholic acid
- Chemistry:Ciclosporin
- Chemistry:Cilengitide
- Biology:Ciltacabtagene autoleucel
- Chemistry:Cipaglucosidase alfa
- Chemistry:Cladribine
- Chemistry:Clofazimine
- Chemistry:Cobicistat
- Chemistry:Cobimetinib
- Chemistry:Colchicine
- Chemistry:Collagenase clostridium histolyticum
- Chemistry:Copper (64Cu) oxodotreotide
- Biology:Crizanlizumab
- Chemistry:Cromoglicic acid
- Chemistry:Cysteamine
D
- Chemistry:Dabrafenib
- Chemistry:Dacomitinib
- Chemistry:Daratumumab
- Chemistry:Darbepoetin alfa
- Biology:Darvadstrocel
- Chemistry:Dasatinib
- Chemistry:Dasiglucagon
- Chemistry:Deferasirox
- Chemistry:Defibrotide
- Chemistry:Depatuxizumab mafodotin
- Chemistry:Development of analogs of thalidomide
- Chemistry:Diflunisal
- Chemistry:Dimethyl fumarate
- Chemistry:Donislecel
- Chemistry:DOTA-TATE
- Biology:Doxorubicin
- Chemistry:Durvalumab
- Chemistry:Duvelisib
E
- Chemistry:Eculizumab
- Chemistry:Edaravone
- Chemistry:Efgartigimod alfa
- Chemistry:Eflornithine
- Biology:Eladocagene exuparvovec
- Chemistry:Elafibranor
- Chemistry:Elapegademase
- Chemistry:Elesclomol
- Chemistry:Elexacaftor
- Biology:Elivaldogene autotemcel
- Chemistry:Elotuzumab
- Chemistry:Elranatamab
- Chemistry:Eltrombopag
- Chemistry:Emapalumab
- Chemistry:Enasidenib
- Chemistry:Encorafenib
- Chemistry:Entinostat
- Chemistry:Entrectinib
- Chemistry:Enzastaurin
- Chemistry:Epcoritamab
- Chemistry:Eplontersen
- Chemistry:Eribulin
- Chemistry:Erlotinib
- Chemistry:Estetrol
- Biology:Etranacogene dezaparvovec
- Chemistry:Everolimus
- Chemistry:Evinacumab
- Biology:Exagamglogene autotemcel
F
- Chemistry:Fasudil
- Chemistry:Fecal microbiota
- Biology:Fecal microbiota spores, live
- Chemistry:Fedratinib
- Chemistry:Fenfluramine
- Chemistry:Fenobam
- Chemistry:Fexinidazole
- Chemistry:Fidarestat
- Chemistry:Fidaxomicin
- Medicine:Fish oil (medical use)
- Chemistry:Florbetaben (18F)
- Chemistry:Flucytosine
- Chemistry:Fomivirsen
- Chemistry:Fosdenopterin
- Chemistry:Fostamatinib
G
- Chemistry:Gallium scan
- Chemistry:Ganaxolone
- Biology:Ganaxolone
- Chemistry:Gemtuzumab ozogamicin
- Chemistry:Gilteritinib
- Biology:Givinostat
- Chemistry:Givosiran
- Biology:Givosiran
- Chemistry:Glasdegib
- Chemistry:Glofitamab
- Chemistry:Glucarpidase
- Chemistry:Glutamine
- Chemistry:Golodirsen
- Biology:Golodirsen
- Chemistry:Gusperimus
I
- Chemistry:Ibalizumab
- Chemistry:Ibrutinib
- Chemistry:Ibutamoren
- Chemistry:Icatibant
- Chemistry:Idebenone
- Biology:Idecabtagene vicleucel
- Biology:Iduronidase
- Chemistry:Idursulfase
- Chemistry:Iloprost
- Chemistry:Imatinib
- Chemistry:Imiglucerase
- Chemistry:Imlifidase
- Chemistry:Immunomodulatory imide drug
- Biology:Inclisiran
- Chemistry:Inebilizumab
- Chemistry:Infigratinib
- Biology:Inotersen
- Chemistry:Iptacopan
- Chemistry:IRGD
- Chemistry:Isatuximab
- Chemistry:Istiratumab
- Chemistry:Itolizumab
- Chemistry:Itraconazole
- Chemistry:Ivacaftor
- Chemistry:Ivosidenib
- Chemistry:Ixazomib