Category:Orphan drugs
From HandWiki
Here is a list of articles in the Orphan drugs category of the Chemistry portal.
Lists of all drugs that have received orphan status in the United States and Europe are available from the U.S. Food and Drug Administration and the European Commission, respectively:
- FDA List of Orphan Designations and Approvals
- European Commission Register of designated Orphan Medicinal Products
Pages in category "Orphan drugs"
The following 200 pages are in this category, out of 472 total.
(previous page) (next page)A
- Biology:Acalabrutinib
- Chemistry:Acetohydroxamic acid
- Chemistry:Acoramidis
- Chemistry:Adagrasib
- Chemistry:Afamelanotide
- Chemistry:Afamitresgene autoleucel
- Chemistry:Afatinib
- Chemistry:Afegostat
- Chemistry:Aficamten
- Chemistry:Alectinib
- Chemistry:Alglucosidase alfa
- Chemistry:Alisporivir
- Chemistry:Alpha-1 antitrypsin
- Chemistry:Altretamine
- Chemistry:Alvocidib
- Chemistry:Amatuximab
- Chemistry:Ambrisentan
- Chemistry:Amifampridine
- Chemistry:Amikacin
- Chemistry:4-Aminopyridine
- Chemistry:Amitriptyline
- Chemistry:Anagrelide
- Chemistry:Ansuvimab
- Chemistry:Anti-CD22 immunotoxin
- Chemistry:Artesunate
- Biology:Arylsulfatase B
- Biology:Asfotase alfa
- Chemistry:Ataluren
- Chemistry:Atezolizumab
- Biology:Atidarsagene autotemcel
- Chemistry:Avacopan
- Chemistry:Avapritinib
- Chemistry:Avatrombopag
- Chemistry:Avelumab
- Chemistry:Axatilimab
- Biology:Axicabtagene ciloleucel
- Chemistry:Azacitidine
B
- Chemistry:Bardoxolone methyl
- Chemistry:Belantamab mafodotin
- Chemistry:Belimumab
- Chemistry:Belumosudil
- Chemistry:Belzutifan
- Chemistry:Benralizumab
- Biology:Beremagene geperpavec
- Chemistry:Berotralstat
- Biology:Betibeglogene autotemcel
- Chemistry:Bevacizumab
- Chemistry:Binimetinib
- Chemistry:Birch bark
- Chemistry:Birch triterpenes
- Biology:Bis-choline tetrathiomolybdate
- Chemistry:Bleximenib
- Chemistry:Blinatumomab
- Chemistry:Bortezomib
- Chemistry:Bosentan
- Chemistry:Brentuximab vedotin
- Biology:Brexucabtagene autoleucel
- Chemistry:Brigatinib
- Chemistry:Brincidofovir
- Biology:Bromelain (pharmacology)
- Chemistry:Budesonide
- Chemistry:Bulevirtide
- Chemistry:Burosumab
- Chemistry:Busulfan
C
- Chemistry:C-Met inhibitor
- Chemistry:Cabozantinib
- Chemistry:Caffeine citrate
- Chemistry:Calaspargase pegol
- Chemistry:Cannabidiol
- Chemistry:Caplacizumab
- Chemistry:Capmatinib
- Chemistry:Carboprost
- Chemistry:Carglumic acid
- Chemistry:Carmustine
- Chemistry:Catridecacog
- Chemistry:CER-001
- Chemistry:Cereblon E3 ligase modulator
- Chemistry:Cerliponase alfa
- Biology:CGTG-102
- Chemistry:Chlormethine
- Chemistry:Cholic acid
- Chemistry:Cilengitide
- Biology:Ciltacabtagene autoleucel
- Chemistry:Cipaglucosidase alfa
- Chemistry:Cladribine
- Chemistry:Clofazimine
- Chemistry:Cobicistat
- Chemistry:Cobimetinib
- Chemistry:Colchicine
- Chemistry:Collagenase clostridium histolyticum
- Chemistry:Concizumab
- Chemistry:Copanlisib
- Chemistry:Copper (64Cu) oxodotreotide
- Chemistry:Copper histidinate
- Biology:Crizanlizumab
- Chemistry:Cromoglicic acid
- Chemistry:Cysteamine
D
- Chemistry:Dabrafenib
- Chemistry:Dacomitinib
- Medicine:Danicopan
- Chemistry:Daratumumab
- Chemistry:Darbepoetin alfa
- Biology:Darvadstrocel
- Chemistry:Dasatinib
- Chemistry:Dasiglucagon
- Chemistry:Deferasirox
- Chemistry:Defibrotide
- Chemistry:Depatuxizumab mafodotin
- Chemistry:Development of analogs of thalidomide
- Chemistry:Diflunisal
- Chemistry:Dimethyl fumarate
- Chemistry:Donidalorsen
- Chemistry:Dordaviprone
- Chemistry:DOTA-TATE
- Chemistry:Durvalumab
- Chemistry:Duvelisib
E
- Chemistry:Eculizumab
- Chemistry:Edaravone
- Chemistry:Efgartigimod alfa
- Chemistry:Eflornithine
- Biology:Eladocagene exuparvovec
- Chemistry:Elafibranor
- Chemistry:Elamipretide
- Chemistry:Elapegademase
- Chemistry:Elesclomol
- Chemistry:Elexacaftor
- Biology:Elivaldogene autotemcel
- Chemistry:Elotuzumab
- Chemistry:Elranatamab
- Chemistry:Eltrombopag
- Chemistry:Emapalumab
- Chemistry:Enasidenib
- Chemistry:Encorafenib
- Chemistry:Entinostat
- Chemistry:Entrectinib
- Chemistry:Enzastaurin
- Chemistry:Epcoritamab
- Chemistry:Eplontersen
- Chemistry:Eribulin
- Chemistry:Erlotinib
- Chemistry:Estetrol
- Biology:Etranacogene dezaparvovec
- Chemistry:Etuvetidigene autotemcel
- Chemistry:Everolimus
- Chemistry:Evinacumab
- Biology:Exagamglogene autotemcel
F
- Chemistry:Fasudil
- Chemistry:Fecal microbiota
- Chemistry:Fedratinib
- Chemistry:Fenfluramine
- Chemistry:Fenobam
- Chemistry:Fexinidazole
- Chemistry:Fidarestat
- Chemistry:Fidaxomicin
- Medicine:Fish oil (medical use)
- Chemistry:Fitusiran
- Chemistry:Flavin mononucleotide
- Chemistry:Florbetaben (18F)
- Chemistry:Flucytosine
- Chemistry:Fomivirsen
- Chemistry:Fosdenopterin
- Chemistry:Fostamatinib
G
- Chemistry:Gallium scan
- Medicine:Gallium scan
- Chemistry:Ganaxolone
- Biology:Ganaxolone
- Chemistry:Garadacimab
- Chemistry:Gemtuzumab ozogamicin
- Chemistry:Gilteritinib
- Biology:Givinostat
- Chemistry:Givosiran
- Biology:Givosiran
- Chemistry:Glasdegib
- Chemistry:Glucarpidase
- Chemistry:Glutamine
- Chemistry:Golodirsen
- Biology:Golodirsen
- Chemistry:Gusperimus
I
- Chemistry:Ibalizumab
- Chemistry:Ibrutinib
- Chemistry:Ibutamoren
- Chemistry:Icatibant
- Chemistry:Idebenone
- Biology:Idecabtagene vicleucel
- Biology:Iduronidase
- Chemistry:Idursulfase
- Chemistry:Iloprost
- Chemistry:Imatinib
- Chemistry:Imetelstat
- Chemistry:Imiglucerase
- Chemistry:Imlifidase
- Chemistry:Immunomodulatory imide drug
- Biology:Inclisiran
- Chemistry:Inebilizumab
- Chemistry:Inotuzumab ozogamicin
- Chemistry:Iptacopan